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2 August 2016 | By Abeona Therapeutics Inc
Abeona Therapeutics provides an update on its first Sanfilippo patient and reports that early biopotency signals suggest a reduction of heparan sulfate in the urine of patients and if confirmed will suggest that intravenous administration of ABO-102 may ultimately provide both central nervous system and systemic benefits to patients...
11 May 2016 | By Victoria White, Digital Content Producer
University of Manchester and CMFT researchers are to work with Orchard Therapeutics to test a stem cell gene therapy for Sanfilippo disease in a human trial...
10 March 2016 | By Victoria White, European Pharmaceutical Review
In the latest issue of European Pharmaceutical Review, the Kaiser Associates European Healthcare team predict four trends to transform healthcare in 2016. We've created an infographic highlighting their key predictions...
Mega mergers, 3D printed drugs, a call for action on antimicrobial resistance: 2015 certainly was an interesting year for the pharmaceutical industry. Here we pick a selection of the top stories that hit the headlines.
3 July 2015 | By Victoria White
A therapy that replaces the faulty gene responsible for cystic fibrosis in patients' lungs has produced encouraging results in a major UK trial...
26 June 2015 | By Victoria White
The number of deals in the global gene therapy market more than doubled in 2014, with their combined value rising spectacularly to $4.9...
