Ricardo Marek

Regulating therapies for rare diseases – recent approvals

This article summarises some of the recent notable drug approvals…

8 August 2024 | By Catherine Eckford (European Pharmaceutical Review)

This article summarises some of the recent notable drug approvals in the EU and US, including a gene therapy and an enzyme replacement therapy.

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Ricardo Marek

Regulating therapies for rare diseases – recent approvals