Dr Julie Beitz

FDA approves Palynziq for PKU, a rare and serious genetic disease

Novel enzyme therapy for adults with PKU who have uncontrolled…

28 May 2018 | By European Pharmaceutical Review

Novel enzyme therapy for adults with PKU who have uncontrolled blood phenylalanine concentrations with current treatment...

news

FDA approves first therapy for rare inherited form of rickets, x-linked hypophosphatemia

The FDA has approved Crysvita, the first drug approved to…

20 April 2018 | By Dr Zara Kassam (European Pharmaceutical Review)

The FDA has approved Crysvita, the first drug approved to treat adults and children ages 1 year and older with x-linked hypophosphatemia, a rare, inherited form of rickets...

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Dr Julie Beitz

FDA approves Palynziq for PKU, a rare and serious genetic disease

FDA approves first therapy for rare inherited form of rickets, x-linked hypophosphatemia