news
Novel medicine could address short stature in children
Some patients had excellent responses in Phase II of an innovative trial of vosoritide in paediatric hypochondroplasia, data shows.
List view / Grid view
BioMarin
news
Ten drugs in pre-registration likely to be blockbusters by 2025, finds report
New research has found that of the drugs in the pre-registration phase, 10 are expected to become blockbusters over the next six years.
news
FDA approves BioMarin’s manufacturing facility in Cork, Ireland
The FDA has approved BioMarin Pharmaceutical’s bulk biologics manufacturing plant, located in Cork, Ireland for production of the formulated bulk substance.
news
NICE draft guidance recommends elosulfase alfa for MPS IVa
23 November 2015 | By Victoria White
The positive draft guidance follows the development of a managed access scheme by BioMarin and NHS England...
news
Pharma companies rank high on Forbes’ most innovative list
19 August 2015 | By Victoria White
Alexion, Regeneron,Incyte and BioMarin have all been ranked in the top ten on Forbes magazine's 2015 list of the "World's Most Innovative Companies"...
news
BioMarin provides programme update for talazoparib in metastatic breast cancer
21 July 2015 | By Victoria White
BioMarin has provided an update on the ABRAZO Phase 2 study of its poly ADP-ribose polymerase (PARP) inhibitor, talazoparib...
news
BioMarin submits MAA for drisapersen for the treatment of Duchenne muscular dystrophy amenable to exon 51 skipping
8 June 2015 | By Victoria White
BioMarin has submitted a MAA for drisapersen for the treatment of the largest subset of Duchenne muscular dystrophy (DMD) amenable to single exon skipping...
news
First treatment for rare genetic condition
29 April 2014 | By BioMarin
The first and only drug designed to address Morquio A syndrome is now available in Europe and the UK for children and adults with this rare genetic condition...
news
BioMarin provides highlights ahead of research and development day
17 September 2013 | By
Members of BioMarin's management team and industry experts will provide an update on the company's product portfolio and advancements in the research and development pipeline...
