Alliance for Regenerative Medicine

CHMP issues positive option for first gene-editing medicine

15 December 2023 | By Caroline Peachey (European Pharmaceutical Review)

If approved, Vertex’s Casgevy (exagamglogene autotemcel) would be the first gene-editing medicine authorised in the European Union.

idea of gene therapy - glowing red DNA strands

article

Many hands make light work: why the new Bespoke Gene Therapy Consortium is a godsend for ambitious biopharma teams

21 December 2021 | By Christian K Schneider (Biopharma Excellence), Christian K Schneider (PharmaLex)

In late October, we learned that an exciting and ambitious new entity – the Bespoke Gene Therapy Consortium (BGTC) – had come into being in the US, designed to encourage the delivery of more gene therapies for rare diseases. The consortium is an interesting construct, headed and funded by the…

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Alliance for Regenerative Medicine

CHMP issues positive option for first gene-editing medicine

Many hands make light work: why the new Bespoke Gene Therapy Consortium is a godsend for ambitious biopharma teams