Rett Syndrome

Astellas invests $50 million in Taysha Gene Therapies

27 October 2022 | By Catherine Eckford (European Pharmaceutical Review)

Taysha will license AAV gene therapy candidates TSHA-102 for Rett syndrome and TSHA-120 for giant axonal neuropathy to Astellas.

news

SB216763 shows efficacy in Rett syndrome

16 May 2018 | By European Pharmaceutical Review

Researchers describe how a new drug is able to reduce the symptoms and activate the dormant neurons characteristic of Rett Syndrome...

news

Newron receives go ahead to test Sarizotan for treatment of Rett Syndrome

18 May 2016 | By Mandy Parrett, Editorial Assistant

Biopharmaceutical company, Newron, has announced that its Investigational New Drug (IND) application to evaluate Sarizotan in treatment of Rett Syndrome has been approved by the FDA.

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Recommended

Rett Syndrome

Astellas invests $50 million in Taysha Gene Therapies

SB216763 shows efficacy in Rett syndrome

Newron receives go ahead to test Sarizotan for treatment of Rett Syndrome