hereditary transthyretin amyloidosis

concept of genome editing - cartoon of a hand using forceps to insert a DNA segment into a larger DNA strand

WHO publishes recommendations on human genome editing

13 July 2021 | By Hannah Balfour (European Pharmaceutical Review)

To promote the safe and ethical use of genome editing for the treatment of disease and genetic disorders WHO has published the first global recommendations.

DNA strands overlaid on test tubes - idea of developing CRISPR therapeutics

news

CRISPR therapies could be one of the most transformative in human history, says GlobalData

16 March 2021 | By Hannah Balfour (European Pharmaceutical Review)

Adam Pearson, Senior Oncology Analyst at GlobalData, comments on the development of CRISPR-based therapies and outlines potential opportunities and challenges in the space.

news

EMA recommends marketing authorisation to Tegsedi for hereditary transthyretin amyloidosis

7 June 2018 | By European Pharmaceutical Review

The EMA has recommended granting a marketing authorisation for Tegsedi, a medicine for the treatment of stage 1 or stage 2 polyneuropathy...

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Recommended

hereditary transthyretin amyloidosis

WHO publishes recommendations on human genome editing

CRISPR therapies could be one of the most transformative in human history, says GlobalData

EMA recommends marketing authorisation to Tegsedi for hereditary transthyretin amyloidosis