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30 September 2015 | By Victoria White
If approved, Translarna would be the first oral protein restoration treatment that targets the underlying cause of nonsense mutation cystic fibrosis...
21 September 2015 | By Roche
Roche announced that new Esbriet® (pirfenidone) data analyses in idiopathic pulmonary fibrosis (IPF) will be presented at the European Respiratory Society (ERS) congress in Amsterdam, 26-30 September 2015...
7 July 2015 | By
Celtaxsys has gained clearance from the US FDA to begin a Phase 2 clinical trial of acebilustat in adult patients with cystic fibrosis (CF) in the US...
3 July 2015 | By Victoria White
The FDA has approved Vertex’s Orkambi, the first medicine to treat the underlying cause of cystic fibrosis in people with two copies of the F508del mutation...
3 July 2015 | By Victoria White
A therapy that replaces the faulty gene responsible for cystic fibrosis in patients' lungs has produced encouraging results in a major UK trial...
18 May 2015 | By Victoria White
Data from two Phase 3 studies of Orkambi, an investigational medicine designed to treat the underlying cause of cystic fibrosis, have been published...
