Cerebral adrenoleukodystrophy (CALD)

CHMP meeting highlights: January 2024

30 January 2024 | By Catherine Eckford (European Pharmaceutical Review)

In its first meeting of 2024, the CHMP recommended a generic medicine for schizophrenia and refused a marketing authorisation (MA) for geographic atrophy.

news

EMA’s human medicines committee (CHMP) meeting highlights, May 2021

24 May 2021 | By Hannah Balfour (European Pharmaceutical Review)

In its latest meeting the CHMP recommended eight medications for approval, 17 medicines for indication extension and concluded reviews of two COVID-19 treatments.

DNA double helix in blue with a specific region (gene) highlighted in yellow - idea of gene therapy

news

bluebird bio releases new data on its gene therapy for cerebral adrenoleukodystrophy

16 March 2021 | By Hannah Balfour (European Pharmaceutical Review)

Data from nearly seven years of follow up suggests one-time treatment with eli-cel may durably stabilise cerebral adrenoleukodystrophy disease progression.

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Recommended

Cerebral adrenoleukodystrophy (CALD)

CHMP meeting highlights: January 2024

EMA’s human medicines committee (CHMP) meeting highlights, May 2021

bluebird bio releases new data on its gene therapy for cerebral adrenoleukodystrophy