William Maier MD PhD (ICON)

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Using RWE in rare disease drug development: effective innovations with historical controls

22 September 2022 | By William Maier MD PhD (ICON)

With a growing number of therapies under development for rare diseases, ICON’s Dr William Maier discusses how real-world evidence (RWE) can be effectively used as a historical control (HC), overcoming challenges presented in clinical development.

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William Maier MD PhD (ICON)

Using RWE in rare disease drug development: effective innovations with historical controls